In this webinar, Juliet Moritz and Benjamen Versano discuss choosing the right Contract Research Organization (CRO) for rare disease programs. They delve into the unique challenges of rare disease research, including the importance of selecting a CRO with experience in small, geographically dispersed patient populations and the need for patient-centric approaches. The presentation provides practical advice on evaluating CROs, focusing on criteria such as regulatory expertise, operational footprint, and patient engagement capabilities to ensure successful partnership and trial execution.
- Selecting the right CRO for rare diseases involves evaluating their experience in rare disease research methodologies and their ability to support patient-centric clinical trials.
- Rare diseases present unique challenges such as small, geographically dispersed patient populations and a lack of natural history data, which can complicate trial recruitment and endpoint selection.
- CROs need to have a robust feasibility process and should demonstrate their ability to engage with key stakeholders, including patients, caregivers, and opinion leaders, to ensure successful study execution.